Hypophosphatemic rickets linked to the X (XLH) chromosome – KRN 23 (burosumab) therapy: expert opinion of the Society for Metabolic Bone Diseases within the Czech Medical Association of J.E. Purkyně
Authors:
Palička Vladimír; Bayer Milan; Rosa Jan; Kutílek Štěpán
Published in the journal:
Clinical Osteology 2018; 23(1): 38-41
Category:
Summary
Received 5. 9. 2018
Zdroje
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Whyte M et al. Burosumab (KRN23), a Fully Human Anti-FGF23 Monoclonal Antibody for X-linked Hypophosphatemia (XLH): Final 64-Week Results of a Randomized, Open-label Phase 2. Study of 52 Children. Oral presentation 1154. The Annual American Society for Bone and Mineral Research Meeting 2017; Denver, CO, USA.
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Carpenter TO et al. Effects of Burosumab (KRN23), a Fully Human Anti-FGF23 Monoclonal Antibody, on Functional Outcomes in Children with X-linked Hypophosphatemia (XLH): Final Results from a Randomized, 64-week, Open-label Phase 2 Study Oral presentation 331. The Annual American Society for Bone and Mineral Research Meeting 2017; Denver, CO, USA.
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Imel EA et al. Oral presentation at the ICCBH 2017; Würzburg, Germany.
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Imel EA et al. The Effects of Burosumab (KRN23), a Fully Human Anti-FGF23 Monoclonal Antibody, on Phosphate Metabolism and Rickets in 1 to 4-Year-Old Children with X-linked Hypophosphatemia (XLH). Oral presentation 695. The Annual American Society for Bone and Mineral Research Meeting 2017; Denver, CO, USA.
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Informace dostupné z WWW: <https://clinicaltrials.gov/ct2/show/NCT02526160>.
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Informace dostupné z WWW: <https://clinicaltrials.gov/ct2/show/NCT02163577>.
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24. Barth JH, Jones RG, Payne RB. Calculation of renal tubular reabsorption of phosphate: the algorithm performs better than the nomogram. Ann Clin Biochem 2000; 37(Pt 1): 79–81.
Štítky
Clinical biochemistry Paediatric gynaecology Paediatric radiology Paediatric rheumatology Endocrinology Gynaecology and obstetrics Internal medicine Orthopaedics General practitioner for adults Radiodiagnostics Rehabilitation Rheumatology Traumatology OsteologyČlánok vyšiel v časopise
Clinical Osteology
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